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The research program is an open label, expanded access program which intends to provide US children, adolescents, and/or adult patients with DMD access to treatment with deflazacort who are ineligible, unable, or otherwise unwilling to enroll in a clinical study examining the efficacy of deflazacort while a marketing application is under preparation and review. In addition, this research program will collect long-term safety and tolerability data from participants.
Who may be Eligible
Patients with DMD who are = 5 years old and are unable or unwilling to participate in any other clinical studies examining how deflazacort works.