Research and Clinical Trials

Deflazacort MP-104-CL-037
Brief Description  
The research program is an open label, expanded access program which intends to provide US children, adolescents, and/or adult patients with DMD access to treatment with deflazacort who are ineligible, unable, or otherwise unwilling to enroll in a clinical study examining the efficacy of deflazacort while a marketing application is under preparation and review. In addition, this research program will collect long-term safety and tolerability data from participants.
Who may be Eligible  
Patients with DMD who are = 5 years old and are unable or unwilling to participate in any other clinical studies examining how deflazacort works.
Start Date  
IRB Number  
Principal Investigator  
Bravver, Elena
Contact Name  

For More Information, Contact   Allison  Newell-Sturdivant , RN
Phone:  (704) 355-5285  Fax:  (704) 446-0840 
Address:  Neurosciences Institute, Neurology-Charlotte
1010 Edgehill Road North
Charlotte, NC 28207